AAV-mediated gene augmentation therapy of CRB1 patient-derived retinal organoids restores the histological and transcriptional retinal phenotype
- Nanda Boon
- , Xuefei Lu
- , Charlotte A Andriessen
- , Ioannis Moustakas
- , Thilo M Buck
- , Christian Freund
- , Christiaan H Arendzen
- , Stefan Böhringer
- , Jan Wijnholds
- , Hailiang Mei
Research output: Contribution to journal/periodical › Article › Scientific › peer-review
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